New orphan drugs

July 24, 2015

The Therapeutic Goods Administration has added Translarna (atalauren) and Cystadrops (mercaptamine hydrochloride) to its list of designated orphan drugs. Translarna is indicated for the treatment of patients with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene, while Cystadrops eye drops solution is for the treatment of corneal cystine deposits in cystinosis.

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Pharmacy DailyPharmacy Daily | New orphan drugs

New orphan drugs

Other recent headlines

Prescribing endorsement consultation opens

Call for embedded rural pharmacist pilot

MTick: Behind the menopause ‘one-stop shop’

SEARCH PHARMACY DAILY

Featured video

Recent issues

INDUSTRY JOB VACANCIES